Mavacamten by Bristol-Myers Squibb is a new breath for all patients with obstructive hypertrophic cardiomyopathy.
FDA
Posted inAutoimmune Diseases, New Drugs, Rare/Orphan Diseases, Regulatory
Tepezza: First Drug for Thyroid Eye Disease
Teprotumumab by Horizon Therapeutics can really help with proptosis and diplopia in Graves’ disease and beyond.
Posted inNew Drugs, Rare/Orphan Diseases, Regulatory
Vijoice: First Targeted Treatment for PIK3CA-Related Overgrowth Spectrum (PROS)
Novartis and its alpelisib will help with very rare diseases with malformations and excessive tissue growth.
Posted inNeuroscience, New Drugs, Regulatory
Igalmi: New Drug for Agitation in Schizophrenia and Bipolar Disorder
BioXcel Therapeutics has offered a fast-action mouth-dissolving sublingual film formulation of dexmedetomidine.
Posted inMetabolism, New Drugs, Regulatory
Kerendia: New Drug for Diabetic Kidney Disease
Finerenone for the treatment of diabetic nephropathy, a chronic kidney disease associated with type 2 diabetes mellitus.
Posted inAutoimmune Diseases, New Drugs, Rare/Orphan Diseases, Regulatory
Enjaymo: First Drug to Treat Cold Agglutinin Disease
Sutimlimab will reduce the need for red blood cell transfusion due to hemolysis.
Posted inAutoimmune Diseases, New Drugs, Rare/Orphan Diseases, Regulatory
Tavneos: New Drug for ANCA-Associated Vasculitis
Avacopan is better than prednisone in the treatment of granulomatosis with polyangiitis and microscopic polyangiitis.