Ensitrelvir by Shionogi & Co. is a highly effective antiviral drug that works just as well as Pfizer’s Paxlovid.
New Drugs
Novel drugs approved by regulators for human use.
A drug is positioned as new if it:
- offers treatment for a disease for which no specific therapy previously existed
- targets a new therapeutic target
- has a new mechanism of action
- is developed in a new formulation, optimized or improved
- is part of a new combination drug
- belongs to a new class of drug compounds.
Posted inNeuroscience, New Drugs, Rare/Orphan Diseases, Regulatory
Relyvrio/Albrioza: New Drug for Amyotrophic Lateral Sclerosis Treatment
Amylyx Pharmaceuticals proposed mixture of sodium phenylbutyrate and tauroursodeoxycholic acid for ALS treatment.
Posted inNeuroscience, New Drugs, Rare/Orphan Diseases, Regulatory
Skysona: Gene Therapy for Cerebral Adrenoleukodystrophy
A single dose of the elivaldogene autotemcel will cure a deadly disease.
Posted inInfections, New Drugs, Regulatory
Beyfortus: Effective Protection for Infants Against Respiratory Syncytial Virus
One injection of nirsevimab reliably protects newborns against the development of RSV-associated lower respiratory tract infections.
Posted inNew Drugs, Rare/Orphan Diseases, Regulatory
Roctavian: Gene Therapy for Hemophilia A
A single infusion of valoctocogene roxaparvovec can completely cure severe hemophilia A.
Posted inNew Drugs, Rare/Orphan Diseases, Regulatory
Zynteglo: Gene Therapy for Beta-thalassemia
One dose of betibeglogene autotemcel will permanently eliminate the dependence on regular blood transfusions.
Posted inAutoimmune Diseases, New Drugs, Regulatory
Sotyktu: Miracle Pill for Autoimmune Diseases
Deucravacitinib by Bristol-Myers Squibb can help with psoriasis, psoriatic arthritis, Crohn’s disease, ulcerative colitis, and systemic lupus erythematosus.