Amylyx Pharmaceuticals proposed mixture of sodium phenylbutyrate and tauroursodeoxycholic acid for ALS treatment.
amyotrophic lateral sclerosis (ALS)
Posted inClinical Trials, Neuroscience, Rare/Orphan Diseases
Qalsody: New Drug for Amyotrophic Lateral Sclerosis with SOD1 Mutation
Tofersen and the mixed results of treatment for the deadly neurodegenerative disease.
Posted inClinical Trials, Neuroscience, Rare/Orphan Diseases
Alsitek: New Drug for ALS
Oral masitinib doubles the life in patients with amyotrophic lateral sclerosis.
Posted inNeuroscience, New Drugs, Regulatory
Oligomannate: Finally New Drug to Treat Alzheimer’s Disease
Innovative Chinese medicine eliminates gut microbiota dysbiosis, and it helps slow the progression of dementia in Alzheimer’s disease.
Posted inAutoimmune Diseases, New Drugs, Rare/Orphan Diseases, Regulatory
Empaveli: Powerful New Drug for Paroxysmal Nocturnal Hemoglobinuria
Pegcetacoplan is more effective in treating paroxysmal nocturnal hemoglobinuria compared to Soliris.
Posted inAutoimmune Diseases, Mergers & Acquisitions, Rare/Orphan Diseases
AstraZeneca + Alexion = Rescue of Both Companies
Alexion Pharmaceuticals, which owns Soliris, one of the most expensive drugs on Earth, has agreed to sell AstraZeneca for $39 billion.