Trastuzumab deruxtecan, developed by AstraZeneca and Daiichi Sankyo, will save lives when Herceptin, Perjeta, and Kadcyla haven’t worked.
FDA
Posted inNew Drugs, Rare/Orphan Diseases, Regulatory
Arcalyst: World’s First Drug to Treat Recurrent Pericarditis
Rilonacept by Kiniksa Pharmaceuticals will reduce recurrent pericarditis to almost nothing.
Posted inNew Drugs, Rare/Orphan Diseases, Regulatory
Zynteglo: Gene Therapy for Beta-thalassemia
One dose of betibeglogene autotemcel will permanently eliminate the dependence on regular blood transfusions.
