A single dose of the elivaldogene autotemcel will cure a deadly disease.
A single infusion of valoctocogene roxaparvovec can completely cure severe hemophilia A.
One dose of betibeglogene autotemcel will permanently eliminate the dependence on regular blood transfusions.
The combination drug will help almost all cystic fibrosis patients.
Krystal Biotech’s beremagene geperpavec gene therapy will save from imminent death.
Human cells are needed for scientific research, development of new drugs, and creation of cell therapies.
Novartis revealed the most expensive drug in the world. And it is amazing.