Nusinersen for the treatment of spinal muscular atrophy will get a follow-up.
PTC Therapeutics
Posted inNeuroscience, New Drugs, Rare/Orphan Diseases, Regulatory
Zolgensma: Gene Therapy That Cure Spinal Muscular Atrophy. The Most Comprehensive Review
Novartis revealed the most expensive drug in the world. And it is amazing.
