Oral givinostat delays the progression of DMD.
Regulatory
Actions of government agencies regulating the pharmaceutical industry: approval, rejection, and prohibition of drugs, granting special statuses.
Tevimbra: Immuno-Oncologic Treatment for Esophageal Cancer
Tislelizumab for the treatment of unresectable or metastatic esophageal squamous cell carcinoma.
Awiqli: Basal Insulin Once a Week
Novo Nordisk invented insulin icodec, a very patient-friendly ultra-long-acting insulin.
Xocova: Powerful New Japanese Pill for Coronavirus Treatment
Ensitrelvir by Shionogi & Co. is a highly effective antiviral drug that works just as well as Pfizer’s Paxlovid.
Relyvrio/Albrioza: New Drug for Amyotrophic Lateral Sclerosis Treatment
Amylyx Pharmaceuticals proposed mixture of sodium phenylbutyrate and tauroursodeoxycholic acid for ALS treatment.
Skysona: Gene Therapy for Cerebral Adrenoleukodystrophy
A single dose of the elivaldogene autotemcel will cure a deadly disease.
Beyfortus: Effective Protection for Infants Against Respiratory Syncytial Virus
One injection of nirsevimab reliably protects newborns against the development of RSV-associated lower respiratory tract infections.