Naxitamab by Y-mAbs Therapeutics offers gorgeous treatment efficacy with unsafe adverse events.
Selumetinib by AstraZeneca powerfully suppresses tumor growth in neurofibromatosis type 1.
Novartis revealed the most expensive drug in the world. And it is amazing.
Rilonacept by Kiniksa Pharmaceuticals will reduce recurrent pericarditis to almost nothing.
One dose of betibeglogene autotemcel will permanently eliminate the dependence on regular blood transfusions.