A single infusion of valoctocogene roxaparvovec can completely cure severe hemophilia A.
EMA
Posted inNew Drugs, Rare/Orphan Diseases, Regulatory
Zynteglo: Gene Therapy for Beta-thalassemia
One dose of betibeglogene autotemcel will permanently eliminate the dependence on regular blood transfusions.
Posted inNew Drugs, Oncology, Rare/Orphan Diseases, Regulatory
Tecvayli: New Drug for Multiple Myeloma
Teclistamab by Johnson & Johnson is a new hope for refractory or relapsing multiple myeloma.
Posted inClinical Trials, Infections, New Drugs, Regulatory
Hepcludex: Effective Treatment for Chronic Hepatitis D
Bulevirtide is the only approved antiviral drug against hepatitis delta.
Posted inCOVID-19, Infections, New Drugs, Regulatory
Covovax/Nuvaxovid: Nanoparticle Vaccine for COVID-19
Covovax/Nuvaxovid by Novavax is a protein subunit vaccine from virus-like particles.
Posted inMetabolism, New Drugs, Regulatory
Kerendia: New Drug for Diabetic Kidney Disease
Finerenone for the treatment of diabetic nephropathy, a chronic kidney disease associated with type 2 diabetes mellitus.